Study Locations

Clinical Trial Study Sites:

If you are interested in participating but do not see a study site in your geography, please contact us at:

or visit
(Identifier: NCT02675465)



United States:

United States, Arizona
Neuromuscular Research Centre Recruiting
Phoenix, Arizona, United States, 85028
Kumaraswamy Sivakumar
480-314-1007 ext 6
Kristy Osgood   
480-314-1007 ext 6
Principal Investigator:
Kumaraswamy Sivakumar         
United States, California
University of California Irvine Active, not recruiting
Orange, California, United States 92868
United States, Florida
University of Florida Active, not recruiting
Gainesville, Florida, United States, 32610
United States, Georgia
Emory University Division of Medical Genetics Completed
Decatur, Georgia, United States, 30033
United States, Michigan
Infusion Associates Active, not recruiting
Grand Rapids, Michigan, United States, 49525
United States, Montana
Great Falls Clinic, LLP Active, not recruiting
Great Falls, Montana, United States, 59405
United States, New Jersey
Rutgers New Jersey Medical School Active, not recruiting
Newark, New Jersey, United States, 08103
United States, North Carolina
Duke University Medical Center Active, not recruiting
Durham, North Carolina, United States, 27710
United States, Pennsylvania
University of Pittsburgh Active, not recruiting
Pittsburgh, Pennsylvania, United States, 15213
United States, Virginia
O&O Alpan LLC Active, not recruiting
Fairfax, Virginia, United States, 22030



Australia, South Australia
Womens & Childrens Hospital, Adelaide Active, not recruiting
North Adelaide, South Australia, Australia, 05006
University Children's Hospital
Active, not recruiting
Department of Neuropediatrics and
Inborn Metabolic Disorders
St. Josefs-Hospital
Bochum, Germany, 44791
Active, not recruiting
Dep of Neurology - University Munich
Munich, Germany, 80336
Erasmus Medical Center Active, not recruiting
Rotterdam, Netherlands
United Kingdom
University Hospital Birmingham Completed
NHS Foundation Trust
Queen Elizabeth Medical Center
Birmingham, United Kingdom, B15 2TH
Salford Royal NHS Foundation Trust Completed
Salford, United Kingdom, M6 8HD